Clinical Trials

An Important Note:
Clinical trials listed for ITP are a starting point for discussion with a healthcare professional. Be sure you understand all the implications of the proposed treatment by reading the informed consent very carefully and speaking with your doctor before enrolling in a clinical trial.

Doctor with patientWhat are Clinical Trials?

Clinical Trials are controlled patient studies that must be performed before a new drug or treatment is approved by the Food and Drug Administration (FDA) in the United States and similar organizations in other countries. Clinical trials are also completed after a drug or treatment is approved to document the effectiveness of the treatment, or to gain approval to use the drug or therapy for a different disease or age group.

There are three main phases to clinical trials, completed in sequence. A Phase I study tests the safety and side effects of the drug. A Phase II study is initiated to determine the efficacy of the drug, to see if it works as anticipated. And, a Phase III study tests the efficacy of drug or treatment and documents the side effects in a large population of volunteers.

Finding a Clinical Trial

The best way to find the latest information on clinical trials is by visiting, a database of privately and publicly funded clinical studies conducted around the world. Pharmaceutical companies and researchers update this site frequently to ensure it contains the most comprehensive and up-to-date clinical trial listings. The database features an easy-to-use search facility and detailed guidance for patients and industry.

Featured Clinical Trials

advance SC+ argenx logoThe ADVANCE + sc trial, a global Phase 3 clinical study testing the efficacy and safety of efgartigimod, an investigational subcutaneous treatment designed to treat the underlying causes of ITP. The ADVANCE + sc study was designed with input from the patients and physicians in an effort to address existing unmet needs in ITP treatment options.

To be eligible, the participants must be at least 18 years old, not be pregnant or lactating and be actively trying to get pregnant. Participants must have been diagnosed with primary ITP for more than 3 months. There are other eligibility criteria which patient advocates and study staff will discuss with you.

The ADVANCE + sq clinical study is sponsored by argenx. Each day at argenx, we are motivated to pursue a better tomorrow alongside patients.

For more information please visit or and search NCT04188379.

List of Clinical Trials

Please contact PDSA if you find missing or incorrect information regarding any of the clinical trials listed.



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